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PYC Therapeutics Advances Four Genetic Disease Programs, Eyes Transformative 2025

9:25am on Wednesday 29th of January, 2025 AEDT Biotechnology
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PYC Therapeutics Advances Four Genetic Disease Programs, Eyes Transformative 2025

9:25am on Wednesday 29th of January, 2025 AEDT
Key Points
  • Phase 1/2 clinical data presented for Retinitis Pigmentosa type 11 showing patient improvement
  • FDA grants Orphan Drug and Rare Pediatric Disease designations for RP11 candidate
  • First dosing completed in Autosomal Dominant Optic Atrophy clinical trial
  • Pre-clinical studies completed and regulatory submission made for Polycystic Kidney Disease program
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