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Can PYC Therapeutics’ RNA Drug Revolutionize Phelan-McDermid Syndrome Treatment?
9:21am on Friday 27th of June, 2025 AEST
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Biotechnology
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Can PYC Therapeutics’ RNA Drug Revolutionize Phelan-McDermid Syndrome Treatment?
9:21am on Friday 27th of June, 2025 AEST
Key Points
PYC-002 restores SHANK3 gene expression in patient-derived neurons
Demonstrated functional neuronal improvements in vitro and in vivo
Effective gene modulation in key brain regions of animal models
Intrathecal delivery designed to bypass the blood-brain barrier
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