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Why Did EMA’s Committee Reject Trofinetide for Rett Syndrome in Europe?

9:50am on Tuesday 3rd of February, 2026 AEDT Pharmaceuticals
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Why Did EMA’s Committee Reject Trofinetide for Rett Syndrome in Europe?

9:50am on Tuesday 3rd of February, 2026 AEDT
Key Points
  • Negative trend vote from EMA’s CHMP on trofinetide EU approval
  • Acadia plans to request re-examination of the opinion
  • Trofinetide already approved in US, Canada, and Israel
  • Over 1,000 patients currently treated globally
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